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Organisation › Details

Spark Therapeutics Inc.

At Spark Therapeutics, a fully integrated, commercial company committed to discovering, developing and delivering gene therapies, we challenge the inevitability of genetic diseases, including blindness, hemophilia, lysosomal storage disorders and neurodegenerative diseases. We have successfully applied our technology in the first FDA-approved gene therapy in the U.S. for a genetic disease, and currently have three programs in clinical trials, including product candidates that have shown promising early results in patients with hemophilia. At Spark, we see the path to a world where no life is limited by genetic disease. *


Period Start 2013-10-01 established
  Group Roche (Group)
  Predecessor Children’s Hospital of Philadelphia (CHOP)
Products Industry gene therapy
  Industry 2 adeno-associated viral vector (AAV vector)
Persons Person Marrazzo, Jeffrey D. (Spark Therapeutics 201811 CEO)
  Person 2 Wright, Fraser (Yposkesi 201807– Senior Advisor before co-founder + CTO of Spark Therapeutics + Avigen)
Region Region Philadelphia, PA
  Country United States (USA)
  Street 3737 Market Street
Suite 1300
  City 19104 Philadelphia, PA
  Tel +1-215-220-9300
    Address record changed: 2020-12-02
Basic data Employees n. a.
    * Document for �About Section�: Spark Therapeutics, Inc.. (11/23/18). "Press Release: European Commission Approves Spark Therapeutics’ Luxturna (voretigene neparvovec), a One-time Gene Therapy for Inherited Retinal Disease Caused by Confirmed Biallelic RPE65 Mutations". Philadeliphia,
Record changed: 2020-11-12


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